Spinraza improved motor function in children and adolescents with SMA in a real-world study from Czechia and Slovakia.

Melatonin and pioglitazone, two approved drugs that act on metabolism, improved motor function and prolonged survival in ...

When it comes to disability inclusion, language is powerful, but it needs to be supported by action, argues columnist Sherry ...

Columnist Connie Chandler shares three things in her life with SMA that she thinks someone who might want to spend time with ...

SMA treatment Evrysdi partly normalized changes in molecules tied to inflammation and cellular stress in adults with ...

Dallas, keynote speaker Lily Sander discusses belonging, resilience, and the power of community and connection.

In getting ready for the day, columnist Connie Chandler's caregiver helps her look good on the outside, but Connie's attitude ...

This Halloween, an 11-year-old living with SMA named Dash will be trick-or-treating in a custom wheelchair costume inspired ...

Connie Chandler is a Christ-focused care and support specialist at the nonprofit organization Joni and Friends. She grew up in the foothills of North Carolina but now owns a home and lives in Fort ...

Treatment with Evrysdi (risdiplam) was associated with stable overall motor function and improved upper limb function in a small Chinese study of 15 people with spinal muscular atrophy (SMA). Upper ...

It started with what I had assumed was an ordinary breakout. I’d been stressed from moving for the first time in my life, and had punted on my typically zealous hygiene because, well, moving. You ...

Spinal muscular atrophy with respiratory distress type 1 (SMARD1 is a rare type of spinal muscular atrophy (SMA) that usually begins with breathing difficulties in infancy and progresses to muscle ...